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📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
This was an open-label, repeat-dose, intra-participant dose-escalation stud...
Status
Completed
Location
Multiple Locations
Start Date
2011-05-04
Trial ID
NCT01371825
Treatments Being Tested
This was an open-label, repeat-dose, study of sebelipase alfa in infants wi...
Status
Terminated
Location
Multiple Locations
Start Date
2014-06-06
Trial ID
NCT02193867
Treatments Being Tested
This is an open-label, multicenter expanded access protocol to allow patien...
Status
No Longer Available
Location
Multiple Locations
Start Date
TBD
Trial ID
NCT02376751
Treatments Being Tested
This was the first clinical study of SBC-102 (sebelipase alfa) for the trea...
Status
Completed
Location
Multiple Locations
Start Date
2011-04-25
Trial ID
NCT01307098
Treatments Being Tested
The primary outcome of this study is the development of a clinical profile ...
Status
Terminated
Location
Children's Healthcare of Atlanta
Start Date
2016-11
Trial ID
NCT02926872
Treatments Being Tested
This was an extension study to Study LAL-CL01 (NCT01307098). The primary ob...
Status
Completed
Location
Multiple Locations
Start Date
2011-12-12
Trial ID
NCT01488097
Treatments Being Tested
For detailed information, please view our study website: https://pearltrial...
Status
Recruiting
Location
University of California
Start Date
2021-07-01
Trial ID
NCT04532047
Treatments Being Tested
This Phase 3 study evaluated the efficacy and safety of 1 milligram/kilogra...
Status
Completed
Location
Multiple Locations
Start Date
2013-01-22
Trial ID
NCT01757184
Treatments Being Tested
This study evaluated the safety and efficacy of sebelipase alfa in a broad ...
Status
Completed
Location
Multiple Locations
Start Date
2014-06-24
Trial ID
NCT02112994
Treatments Being Tested